§ 08 · domain
Specialized Therapeutic Modalities
Antibody-drug conjugates
0 tools
Aptamers
1 tools
SELEX + ML hybrid pipelines
RaptGen, AptaTrans, deep-learning-guided SELEX rounds.
Gene editing & delivery
3 tools
AAV capsid engineering
Dyno Therapeutics, Alia Therapeutics use ML-guided design.
CRISPR guide design
DeepCRISPR, CRISPR-Net (mature, widely used).
Lipid nanoparticle optimization
active ML/experimental loops at Acuitas, Moderna, Generate.
PROTACs / molecular glues
3 tools
DegraderDB
curated training data.
Generative PROTAC design
linker optimization is a major bottleneck; multiple groups working on it.
PROTAC-DB
curated training data.
mRNA & vaccines
2 tools
Generative mRNA design
active area at Moderna, BioNTech, Stanford (Das/Hie groups).
LinearDesign
RNA codon optimization for stability and translation efficiency.